Computational analysis of transcriptome signature repurposes low dose trifluoperazine for the treatment of fragile X syndrome in mouse model
Qi Ding, Ferzin Sethna, Xueting Wu, Zhuang Miao, Ping Chen, Yueqi Zhang, Hua Xiao, Wei Feng, Yue Feng, Xuan Li, Hongbing Wang
The paper identifies trifluoperazine as a potential treatment for FXS using transcriptome analysis and experimental validation.
Communications Biology · Mar 16, 2020Peer-reviewedNeuroscience