Near-perfect precise on-target editing of human hematopoietic stem and progenitor cells
F.-M. Cloarec-Ung, J. Beaulieu, A. Suthananthan, B. Lehnertz, G. Sauvageau, H. M. Sheppard, D. J. Knapp
This study achieves near-perfect on-target gene editing in human hematopoietic stem and progenitor cells with high efficiency and minimal off-target effects.
bioRxiv · May 26, 2023Bioengineering