Lipid nanoparticle-mediated delivery of mRNA into the mouse and human retina and other ocular tissues.
C. Chambers, Gillian L. Soo, Abbi L. Engel, Ian A. Glass, Andrea Frassetto, Paolo G.V. Martini, Timothy J. Cherry
This paper demonstrates reliable mRNA delivery via lipid nanoparticles to specific retinal cells in mice and human ocular tissues without significant inflammation.
Translational Vision Science & Technology · Jul 9, 2024Peer-reviewedMolecular Biology