A scalable, clinically severe pig model for Duchenne muscular dystrophy
M. Stirm, L. M. Fonteyne, B. Shashikadze, M. Lindner, M. Chirivi, A. Lange, C. Kaufhold, C. Mayer, I. Medugorac, B. Kessler, M. Kurome, V. Zakhartchenko, A. Hinrichs, E. Kemter, S. Krause, , E. Wolf
This paper develops a scalable pig model for Duchenne muscular dystrophy by breeding DMD carriers, enabling large cohorts for disease mechanism studies and therapeutic testing.
Disease Models & Mechanisms · Dec 1, 2021Peer-reviewedPathology