Mitochondrial adenine base editing of mouse somatic tissues via adeno-associated viral delivery
Christian Daniel Mutti, Lindsey Van Haute, Lucia Luengo-Gutierrez, Isabel Dowling, Jose Domingo Barrera-Paez, Keira Turner, Pedro Silva-Pinheiro, Michal A. Minczuk
This study tests mitochondrial adenine base editing in mouse tissues via AAV delivery, finding low and modestly increasing editing efficiency over time.
bioRxiv · Dec 10, 2024 · PreprintBioengineering