MECP2-mutant marmosets exhibit primate-specific phenotypes of Rett syndrome
Noriyuki Kishi, Junko Okahara, Kenya Sato, Daisuke Yoshimaru, Yoko Kurotaki, Kohei Onishi, Tsukasa Sanosaka, Rachel Henry, Taeko Ito, Misako Okuno, Edward J. Weinstein, Jill R. Crittenden, Hirotaka James Okano, Jun-ichi Hata, Jun Kohyama, , Hideyuki Okano
This study generates MECP2-knockout marmosets to model Rett syndrome, revealing cortical structural and gene expression changes linked to the disease.
bioRxiv · Jun 29, 2026 · PreprintNeuroscience