BioengineeringbioRxiv
Lung and liver editing by lipid nanoparticle delivery of a stable CRISPR-Cas9 RNP
Kai Chen, Hesong Han, Sheng Zhao…·Jennifer A. Doudna
This study demonstrates that lipid nanoparticle-delivered thermostable Cas9 RNPs achieve high-efficiency genome editing in mouse liver and lung tissues.
DOI 10.1038/s41587-024-02437-3