Dual S100A1 and ARC gene therapy as a treatment for DMD cardiomyopathy
David W. Hammers, Cora C. Hart, Young Il Lee, Margaret M. Sleeper, Hugh Lee Sweeney
This paper investigates dual S100A1 and ARC gene therapy for DMD cardiomyopathy, showing improved cardiac function and survival in mouse models and safety in canine models.
bioRxiv · Aug 23, 2025 · PreprintMolecular Biology