CRISPR/Cas9-mediated generation of two isogenic CEP290-mutated iPSC lines
Joana Figueiro‐Silva, Melanie Eschment, Michelle Mennel, Affef Abidi, Beatrice Oneda, Anita M. Rauch, Ruxandra Bachmann-Gagescu
This study generates two isogenic CEP290-mutated iPSC lines using CRISPR/Cas9 for disease modeling of ciliopathies.
Stem Cell Research · Sep 1, 2025Peer-reviewedDevelopmental Biology