Developmental BiologyStem Cell ResearchPeer-reviewed
CRISPR/Cas9-mediated generation of two isogenic CEP290-mutated iPSC lines
Joana Figueiro‐Silva, Melanie Eschment, Michelle Mennel…·Ruxandra Bachmann-Gagescu
This study generates two isogenic CEP290-mutated iPSC lines using CRISPR/Cas9 for disease modeling of ciliopathies.
DOI 10.1016/j.scr.2025.103781