Combination siRNA delivery as a therapeutic strategy for ADPKD
Joshua Giblin, Isabella Suzuki, Yi Huang, Karla Lambaren, Veronica LaMastro, Rowan Simon, Jose Zarate‐Diaz, Ali Osouli, Jessica Pham, Soobeen Laura Bae, Kenneth R. Hallows, Eun Ji Chung
This study demonstrates that dual-target siRNA delivery using CD-targeting micelles reduces cyst growth in ADPKD models by silencing TMEM16A and MCP-1.
bioRxiv · Jul 21, 2026 · PreprintBioengineering