Nonviral PDMAEMA Vectors Efficiently Express PDE6beta in a Mouse Model of Retinitis Pigmentosa
D. B. Bitoque, S. M. Calado, A. M. Rosa da Costa, G. Silva
This study demonstrates that PDMAEMA polyplexes efficiently deliver and express the PDE6beta gene in a mouse model of Retinitis Pigmentosa.
bioRxiv · May 4, 2023 · PreprintBioengineering