Challenges and promises in optimising a non-clinical protocol of intracerebroventricular human neural stem cell transplantation in ALS
Ivan Lombardi, Clelia Ferrero, Edvige Vulcano, Daniela Maria Rasà, Maurizio Gelati, Diego Pastor Campos, Rose Mary Carletti, Silvia de la Morena, Daniela Celeste Profico, Sabrina Longobardi, Elisa Lazzarino, Elisa Perciballi, Jessica Diana Rosati, Salvador Martı́nez, Alessandro Vercelli, , Daniela Ferrari
This study evaluates the safety and efficacy of human neural stem cell transplantation in ALS using immunodeficient mice, finding it safe and showing potential therapeutic benefits with prolonged immunosuppression.
bioRxiv · Nov 18, 2024 · PreprintNeuroscience