AAV-based delivery of RNAi targeting Ataxin-2 improves survival, strength, and pathology in mouse models of rapidly and slowly progressive sporadic ALS
Defne A. Amado, Ashley B. Robbins, Alicia R. Smith, Katherine R. Whiteman, Guillem Chillon Bosch, Yonghong Chen, Joshua A. K. Fuller, Aleksandar Izda, Shareen Nelson, Abigail I Dichter, Alex Mas Monteys, Beverly L. Davidson
bioRxiv · Jan 31, 2024 · PreprintNeuroscience