Author

Susan Gembic

National Institutes of Health

Listed by name: these papers carry no ORCID for this author, so different people with the same name may be mixed together.

Biology Disciplines

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Neuroscience· 1

Signature Assays, Organisms & Methods

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Approach:experimental assay· 1 Organism:mouse· 1

Frequent Co-Authors

Alana L. GibsoniD· 1 shared Arturo A. IncaoiD· 1 shared Avani V. MylvaraiD· 1 shared Charles P. VendittiiD· 1 shared Cristin D. DavidsoniD· 1 shared Dominick Pierre-JacquesiD· 1 shared Forbes D. PorteriD· 1 shared Katerina D MelnykiD· 1 shared

Activity by Year

2026-2026 · peak 1/yr

Co-Author Collaboration Network

10 top collaborators · 45 mutual co-author links

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1 shared paperNeuroscience

Alana L. GibsonORCID

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1 paper

Recent·Most cited

Optimization of systemic AAV9 gene therapy in Niemann-Pick disease type C1 mice

Avani V. Mylvara, Alana L. Gibson, Tansy Gu, Cristin D. Davidson, Arturo A. Incao, Katerina D Melnyk, Susan Gembic, Dominick Pierre-Jacques, Stephanie M. Cologna, Charles P. Venditti, Forbes D. Porter, William J. Pavan

This study evaluates the efficacy of systemic AAV9-hNPC1 gene therapy in NPC1 mouse models, finding that higher doses and earlier treatment improve survival and slow disease progression.

Life Science Alliance · Mar 18, 2026Peer-reviewedNeuroscience