BioengineeringbioRxiv
Human stem cell-based retina-on-chip as new translational model for validation of AAV retinal gene therapy vectors
K. Achberger, M. Cipriano, M. Duechs…·P. Loskill
The paper evaluates seven AAV vectors using a human stem cell-derived Retina-on-chip model to assess their efficacy, kinetics, and cell tropism.
DOI 10.1016/j.stemcr.2021.08.008