Cell BiologybioRxiv
Myospreader improves gene editing in skeletal muscle by myonuclear propagation
K. Poukalov, M. C. Valero, D. Muscato…·E. T. Wang
Myospreader enhances CRISPR/Cas9 gene editing in skeletal muscle by promoting myonuclear propagation and improving therapeutic efficacy in mouse models.
DOI 10.1073/pnas.2321438121