Targeting SUFU-mediated GLI activity alleviates ciliopathic phenotypes
Ching‐Fang Chang, Yanfen Yang, Kari M. Brown, Daniel T. Rasicci, Timothy Nguyen, Kevin A. Peterson, Samantha A. Brugmann
This study shows that modulating SUFU-GLI interactions rescues ciliopathic phenotypes in mice by restoring GLI transcriptional activity without requiring ciliary processing.
bioRxiv · Oct 26, 2026 · PreprintDevelopmental Biology