Developmental BiologybioRxivPreprint
Targeting SUFU-mediated GLI activity alleviates ciliopathic phenotypes
Ching‐Fang Chang, Yanfen Yang, Kari M. Brown…·Samantha A. Brugmann
This study shows that modulating SUFU-GLI interactions rescues ciliopathic phenotypes in mice by restoring GLI transcriptional activity without requiring ciliary processing.
DOI 10.64898/2026.10.23.760487