NeurosciencebioRxivPreprint
Plasma Membrane Remodelling in GM2 Gangliosidoses Drives Synaptic Dysfunction
Alex S. Nicholson, David A. Priestman, Robin Antrobus…·Janet Elwyn Deane
This study develops i3Neuron models of Tay-Sachs and Sandhoff diseases, revealing plasma membrane remodeling and synaptic dysfunction due to GM2 ganglioside accumulation.
3 citations