Molecular BiologyMolecular TherapyPeer-reviewed
Di-valent siRNA Mediated Silencing of MSH3 Blocks Somatic Repeat Expansion in Mouse Models of Huntington's Disease
Daniel O’Reilly, Jillian Belgrad, Chantal M. Ferguson…·Anastasia Khvorova
Silencing MSH3 in the CNS of two models of Huntington's disease using di-valent siRNA blocks disease-accelerating somatic expansion of CAG repeats.
60 citationstop 2%