NeuroscienceScience Translational MedicinePeer-reviewed
Human neurons from Christianson syndrome iPSCs reveal allele-specific responses to rescue strategies
Sofia B. Lizarraga, Li Ma, Abbie M. Maguire…·Eric M. Morrow
The paper uses iPSC-derived neurons from Christianson syndrome patients to show allele-specific responses to rescue strategies, highlighting the need for personalized therapeutic approaches.