NeurosciencebioRxivPreprint
Metformin decreases RAN proteins, rescues splicing abnormalities and improves behavioral phenotypes in SCA8 BAC mice
Lisa E. L. Romano, Setsuki Tsukagoshi, Emily E Davey…·Laura P.W. Ranum
Metformin reduces RAN proteins, improves splicing, and enhances behavioral and neuropathological outcomes in SCA8 BAC mice.
DOI 10.1101/2025.08.21.671563