BioengineeringbioRxivPreprint
Single-AAV CRISPR editing of skeletal muscle in non-human primates with NanoCas, an ultracompact nuclease
Benjamin J. Rauch, Aaron DeLoughery, Renan B. Sper…·Lucas B. Harrington
This paper develops NanoCas, a compact CRISPR nuclease, and demonstrates its efficacy in editing non-liver tissues in non-human primates.
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