NeuroscienceEMBO Molecular MedicinePeer-reviewed
iPSC-based modeling of THD recapitulates disease phenotypes and reveals neuronal malformation
Alba Tristán‐Noguero, Irene Fernández‐Carasa, Carles Calatayud…·Antonella Consiglio
This study uses iPSC-derived dopaminergic neurons to model THD, showing disease-specific phenotypes and treatment responses.
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