GenomicsbioRxivPreprint
Large-scale discovery of potent, compact and lineage specific enhancers for gene therapy vectors
Nikoletta Psatha, Pavel Sova, Grigorios Georgolopoulos…·Jeff D. Vierstra
The paper identifies potent, compact, and lineage-specific enhancers for gene therapy vectors using epigenomic data and validates their efficacy in correcting a thalassemia phenotype.
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