Correction of β3 integrin haplo-insufficiency by CRISPRa normalizes cortical network activity
Fanny Jaudon, Agnes Thalhammer, Lorenzo A. Cingolani
This study uses CRISPRa to correct β3 integrin haplo-insufficiency in neurons, rebalancing network activity without causing hyperactivity seen with exogenous gene expression.
bioRxiv · Jun 10, 2019 · PreprintNeuroscience