GeneticsbioRxivPreprint
Bystander base editing interferes with visual function restoration in Leber congenital amaurosis
Seok‐Hoon Lee, Jun Wu, Dongjoon Im…·Sangsu Bae
The paper shows that bystander base editing with ABE8e impairs visual function restoration in LCA model mice by causing structural and functional disruptions in RPE65.
3 citations