GeneticsbioRxivPreprint
Synergistic effect of deoxynucleosides and AAV gene therapy for thymidine kinase 2 deficiency
Carlos Lopez Gomez, Maria J. Sanchez‐Quintero, Eung Jeon Lee…·Michio Hirano
This study shows that combining AAV gene therapy with deoxynucleoside supplementation improves survival and mitochondrial function in Tk2-deficient mice.
DOI 10.1101/2020.10.08.330969