Mitochondrial genome microhomology-mediated editing by donor DNA delivery into mitochondria in human cells.
V.N. Maximov Maximov, Nikita Shebanov, Natalia Nikitchina, Rachel Rapoport, Yehoshua Maor, Ivan Tarassov, Ophry Pines, Nina Entelis
This paper introduces a method for editing mitochondrial DNA using donor DNA and microhomology-mediated end joining, achieving targeted nucleotide changes in human cells.
Molecular Therapy — Nucleic Acids · May 19, 2026Peer-reviewedMolecular Biology