GeneticsMolecular Therapy — Methods & Clinical DevelopmentPeer-reviewed
Preclinical evaluation of the efficacy and safety of AAV1-hOTOF in mice and non-human primates
Longlong Zhang, Hui Wang, Mengzhao Xun…·Yilai Shu
This study evaluates the efficacy and safety of AAV1-hOTOF gene therapy in mice and non-human primates for treating DFNB9 hearing loss.
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