Preclinical evaluation of the efficacy and safety of AAV1-hOTOF in mice and non-human primates
Longlong Zhang, Hui Wang, Mengzhao Xun, Honghai Tang, Jinghan Wang, Jun Lv, Biyun Zhu, Yuxin Chen, Daqi Wang, Shaowei Hu, Ziwen Gao, Jianping Liu, Zheng‐Yi Chen, Bing Chen, Huawei Li, Yilai Shu
This study evaluates the efficacy and safety of AAV1-hOTOF gene therapy in mice and non-human primates for treating DFNB9 hearing loss.
Molecular Therapy — Methods & Clinical Development · Nov 10, 2023Peer-reviewedGenetics