Rewriting endogenous human transcripts with trans-splicing
Sita S. Chandrasekaran, Cyrus Tau, Matthew Nemeth, April Pawluk, Silvana Konermann, Patrick D. Hsu
This paper introduces RESPLICE, a CRISPR-based trans-splicing system that efficiently edits endogenous human transcripts, achieving up to 90% trans-splicing efficiency in sorted cells.
bioRxiv · Jan 29, 2024 · PreprintMolecular Biology