Molecular BiologyMolecular Therapy — Methods & Clinical DevelopmentPeer-reviewed
Optimization of AAV6 transduction enhances site-specific genome editing of primary human lymphocytes
Geoffrey L. Rogers, Chun Huang, Robert D.E. Clark…·Paula M. Cannon
This study optimizes AAV6 transduction for ex vivo genome editing of human lymphocytes, achieving higher editing rates with reduced vector usage and toxicity.
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