GeneticsbioRxivPreprint
PAM-flexible adenine base editing rescues hearing loss in a humanized MPZL2 mouse model harboring an East Asian founder mutation
Shao Wei Hu, Sohyang Jeong, Luoying Jiang…·Yilai Shu
This study uses base editing to correct a mutation causing hearing loss in a humanized mouse model, restoring hearing function and gene expression.
4 citations