Cell-specific CRISPR/Cas9 activation by microRNA-dependent expression of anti-CRISPR proteins
Mareike Daniela Hoffmann, Sabine Aschenbrenner, Stefanie Große, Kleopatra Rapti, Claire Domenger, Julia Fakhiri, Manuel Mastel, Kathleen Börner, Roland Eils, Dirk Grimm, Dominik Niopek
This paper develops a cell-specific CRISPR/Cas9 activation system using miRNA-regulated anti-CRISPR proteins, demonstrating targeted gene activation in liver and muscle cells.
Nucleic Acids Research · Apr 5, 2019Peer-reviewedSynthetic Biology