GeneticsbioRxivPreprint
Nonviral base editing of KCNJ13 mutation preserves vision in an inherited retinal channelopathy
Meha Kabra, Pawan Kumar Shahi, Yuyuan Wang…·Bikash Ranjan Pattnaik
This paper demonstrates nonviral base editing of a KCNJ13 mutation in a mouse model of retinal degeneration, preserving vision through functional rescue of Kir7.1 channels.
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