Duchenne Muscular Dystrophy Cell Culture Models Created By CRISPR/Cas9 Gene Editing And Their Application To Drug Screening
Patricia Soblechero‐Martín, E. Albiasu-Arteta, Aina Anton, Laura de la Puente Ovejero, Iker Garcia-Jimenez, G. González-Iglesias, Irene Larrañaga-Aiestaran, Andrea López‐Martínez, Javier Poyatos‐García, Estibaliz Ruiz-del-Yerro, Federico Gonzãlez, Virginia Arechavala‐Gomeza
The paper describes CRISPR/Cas9-generated Duchenne muscular dystrophy cell models for drug screening, showing successful exon deletion and utrophin upregulation.
Scientific Reports · Sep 14, 2021Peer-reviewedNeuroscience