Inhibition of acid ceramidase as a therapeutic strategy for Niemann-Pick C disease
Isabelle Haynes, Simon E. Ward, Dyfyr Heulyn Jones, Emyr Lloyd‐Evans, Helen Waller‐Evans
This study identifies acid ceramidase as a potential therapeutic target for Niemann-Pick C disease by reducing lipid accumulation in a cellular model.
bioRxiv · Nov 13, 2024 · PreprintCell Biology