Ultrasound-enhanced retinal delivery of engineered viral vectors
Schuyler S. Link, Kara Fan, Jesus Adame, Caroline C. Keehn, Benjamin J. Frankfort, Jerzy O. Szablowski
This study evaluates FUS-BRBO for retinal gene delivery, showing AAV.FUS.3 achieves 2.1-fold and 19.5-fold higher transduction than AAV9 in insonated and uninsonated retinas, respectively.
bioRxiv · Jan 4, 2026 · PreprintBioengineering