Ultrasound-enhanced retinal delivery of engineered viral vectors
Schuyler S. Link, Kara Fan, Jesus Adame…·Jerzy O. Szablowski
This study evaluates FUS-BRBO for retinal gene delivery, showing AAV.FUS.3 achieves 2.1-fold and 19.5-fold higher transduction than AAV9 in insonated and uninsonated retinas, respectively.