BioengineeringbioRxiv
A versatile, high-efficiency platform for CRISPR-based gene activation
A. J. Heidersbach, K. M. Dorighi, J. A. Gomez…·B. Haley
This paper introduces a high-efficiency CRISPRa platform combining piggyBac transposon technology and optimized guide RNA scaffolds to enable rapid, stable gene activation in diverse cellular contexts.
DOI 10.1038/s41467-023-36452-w