AAV-delivery of diacylglycerol kinase kappa achieves long-term rescue of Fmr1-KO mouse model deficits of fragile X syndrome
Karima Habbas, Oktay Cakil, Boglárka Zámbó, Ricardos Tabet, Fabrice Riet, Doulaye Dembélé, Jean‐Louis Mandel, Michaël Hocquemiller, Ralph Laufer, Françoise Piguet, Hervé Moine
AAV-delivered FMRP-independent DGKk corrects brain lipid homeostasis and behavioral deficits in Fmr1-KO mice.
bioRxiv · Apr 14, 2021 · PreprintNeuroscience