Four new Duchenne muscular dystrophy mouse models with clinically relevant exon deletions in the human DMD gene
Maaike van Putten, Margot M. L. Linssen, C. Tanganyika-de Winter, Conny M. Brouwers, Jill W. C. Claassens, Nisha E. Verwey, Max Walsh, Tiberiu Loredan Stan, Annemieke M Aartsma-Rus, Peter Hohenstein
The paper develops four humanized DMD mouse models with specific human exon deletions to test exon skipping therapies for Duchenne muscular dystrophy.
Disease Models & Mechanisms · Aug 1, 2026Peer-reviewedNeuroscience