Precision genome-editing with CRISPR/Cas9 in human induced pluripotent stem cells
John Budde, Rita J. Martinez, Simon Hsu, Natalie Wen, Jason Chen, Giovanni Coppola, Alison Goate, Carlos Cruchaga, Celeste M M. Karch
The paper develops a precise CRISPR/Cas9 genome-editing platform for human iPSCs, demonstrating improved editing efficiency and minimal off-target effects.
bioRxiv · Sep 12, 2017 · PreprintGenetics