Precise manipulation of site and stoichiometry of capsid modification enables optimization of functional adeno-associated virus conjugates
Sarah B. Erickson, Quan Thanh Pham, Xiaofu Cao, Jake Glicksman, Rachel E. Kelemen, Seyed Sadegh Shahraeini, Sebastian Bodkin, Zainab Kiyam, Abhishek Chatterjee
This study shows that precise control over the site and stoichiometry of capsid modification in AAV vectors improves retargeting efficiency and activity.
Bioconjugate Chemistry · Dec 16, 2023Peer-reviewedSynthetic Biology