Zebrafish Functional Screening of FDA-Approved Drugs for Autosomal Dominant Retinitis Pigmentosa Caused by RHODOPSIN Q344X Mutation
Beichen Wang, Logan C. Ganzen, Emre Coskun, Rebecca James, Truc Kha, Xiaoguang Zhu, Jillian A. New, Motokazu Tsujikawa, Yuk Fai Leung
This study screens FDA-approved drugs in a zebrafish model of autosomal dominant retinitis pigmentosa, identifying four compounds that improve visual behavior by distinct mechanisms.
bioRxiv · May 6, 2026 · PreprintNeuroscience