Zebrafish Functional Screening of FDA-Approved Drugs for Autosomal Dominant Retinitis Pigmentosa Caused by RHODOPSIN Q344X Mutation
Beichen Wang, Logan C. Ganzen, Emre Coskun…·Yuk Fai Leung
This study screens FDA-approved drugs in a zebrafish model of autosomal dominant retinitis pigmentosa, identifying four compounds that improve visual behavior by distinct mechanisms.