Myospreader improves gene editing in skeletal muscle by myonuclear propagation
K. Poukalov, M. C. Valero, D. Muscato, L. Adams, H. Chun, Y. i. T. Lee, N. Andrade, Z. Zeier, H. L. Sweeney, E. T. Wang
Myospreader enhances CRISPR/Cas9 gene editing in skeletal muscle by promoting myonuclear propagation and improving therapeutic efficacy in mouse models.
bioRxiv · Nov 6, 2023Cell Biology