Improved split prime editors enable efficient in vivo genome editing
Rong Wei, Zhenxing Yu, Lihong Ding, Zhike Lu, Keyi Yao, Heng Zhang, Binglin Huang, Miao He, Lijia Ma
This study identifies an efficient split site for prime editors and demonstrates improved in vivo genome editing efficiency using dual-AAV delivery in mice.
Cell Reports · Dec 31, 2024Peer-reviewedGenomics